Gene therapy for severe combined immune deficiency poised for European approval: If green-lighted, Strimvelis would provide additional treatment option for second most common form of disease

Am J Med Genet A. 2016 Aug;170(8):1955-6. doi: 10.1002/ajmg.a.37752.
No abstract available

MeSH terms

  • Adenosine Deaminase / genetics
  • Europe
  • Genetic Therapy*
  • Humans
  • Severe Combined Immunodeficiency / therapy*

Substances

  • Adenosine Deaminase