Monitoring Therapy during Treatment of von Willebrand Disease

Semin Thromb Hemost. 2017 Apr;43(3):338-354. doi: 10.1055/s-0036-1585080. Epub 2016 Jul 29.

Abstract

von Willebrand factor (VWF) is an adhesive plasma protein that primarily acts to bridge platelets to sites of vascular injury and thus prevent bleeding. von Willebrand disease (VWD) is the most common inherited bleeding disorder and is caused by deficiency and/or defects of VWF, leading to low levels of plasma VWF or dysfunctional VWF. Factor VIII (FVIII) is also reduced in many patients with VWD, since VWF stabilizes and protects FVIII from degradation. Treatment of VWD primarily entails replacement of VWF, and sometimes FVIII, to protect against bleeding. This may entail use of VWF/FVIII concentrates, and/or desmopressin (1-deamino-8-d-arginine vasopressin) to release endogenous VWF in some patients. Adjunct therapies include antifibrinolytics and hormonal therapies in women. Optimal treatment of VWD entails measuring the effects of treatment, either as a trial before surgery or during therapeutic management. This is usually accomplished by performance of the same tests that are used to help diagnose VWD, although additional monitoring (clinically and/or by laboratory testing) may also be performed. The current review provides an overview of the treatment of VWD but is primarily focused on the monitoring of such therapy.

Publication types

  • Review

MeSH terms

  • Coagulants / therapeutic use
  • Deamino Arginine Vasopressin / therapeutic use*
  • Drug Combinations
  • Drug Monitoring / methods*
  • Factor VIII / therapeutic use*
  • Female
  • Hemostatics / therapeutic use
  • Humans
  • Menorrhagia / complications
  • Menorrhagia / drug therapy
  • Treatment Outcome
  • von Willebrand Diseases / complications
  • von Willebrand Diseases / diagnosis
  • von Willebrand Diseases / drug therapy*
  • von Willebrand Factor / therapeutic use*

Substances

  • Coagulants
  • Drug Combinations
  • Hemostatics
  • factor VIII, von Willebrand factor drug combination
  • von Willebrand Factor
  • Factor VIII
  • Deamino Arginine Vasopressin