Primary ciliary dyskinesia: mechanisms and management

Appl Clin Genet. 2017 Sep 19:10:67-74. doi: 10.2147/TACG.S127129. eCollection 2017.

Abstract

Primary ciliary dyskinesia is a genetically heterogeneous disorder of motile cilia that is predominantly inherited in an autosomal-recessive fashion. It is associated with abnormal ciliary structure and/or function leading to chronic upper and lower respiratory tract infections, male infertility, and situs inversus. The estimated prevalence of primary ciliary dyskinesia is approximately one in 10,000-40,000 live births. Diagnosis depends on clinical presentation, nasal nitric oxide, high-speed video-microscopy analysis, transmission electron microscopy, genetic testing, and immunofluorescence. Here, we review its clinical features, diagnostic methods, molecular basis, and available therapies.

Keywords: Kartagener’s syndrome; genetic testing; primary ciliary dyskinesia.

Publication types

  • Review