Hyperactive Factor IX Padua: A Game-Changer for Hemophilia Gene Therapy

Mol Ther. 2018 Jan 3;26(1):14-16. doi: 10.1016/j.ymthe.2017.12.007. Epub 2017 Dec 21.
No abstract available

Publication types

  • Research Support, Non-U.S. Gov't
  • Comment

MeSH terms

  • Factor IX / genetics*
  • Genetic Therapy
  • Hemophilia A*
  • Hemophilia B
  • Humans

Substances

  • factor IX-Padua
  • Factor IX