Measuring success in hemophilia gene therapy using a factor level & outcomes yardstick

Expert Rev Hematol. 2018 Feb;11(2):83-86. doi: 10.1080/17474086.2018.1423961. Epub 2018 Jan 6.
No abstract available

Keywords: Clotting factor; gene therapy; hemophilia; liver transplant; outcomes.

Publication types

  • Editorial

MeSH terms

  • Animals
  • Genetic Therapy / methods*
  • Hemophilia A / genetics*
  • Hemophilia A / therapy*
  • Humans