Compassionate use of human recombinant insulin-like growth factor-1 therapy in Friedreich's ataxia
Neurologia (Engl Ed). 2020 Mar;35(2):140-143.
doi: 10.1016/j.nrl.2017.11.004.
Epub 2018 Jan 12.
[Article in
English,
Spanish]
Affiliations
- 1 Unidad de Neuropediatría, Instituto del Niño y del Adolescente, Hospital Clínico San Carlos, Madrid, España. Electronic address: adrian.garciar@salud.madrid.org.
- 2 Unidad de Cardiología Infantil, Servicio de Pediatría, Hospital Universitario Infanta Cristina, Parla, Madrid, España.
No abstract available
MeSH terms
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Adolescent
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Compassionate Use Trials*
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Female
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Friedreich Ataxia / drug therapy*
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Friedreich Ataxia / genetics
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Humans
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Insulin-Like Growth Factor I / therapeutic use*
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Ubiquinone / administration & dosage
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Ubiquinone / analogs & derivatives
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Vitamin E / administration & dosage
Substances
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Ubiquinone
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Vitamin E
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Insulin-Like Growth Factor I
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coenzyme Q10
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idebenone