Abstract
Whole exome sequencing detected novel likely pathogenic variants in LRP2 gene in 2 patients presenting with hearing and vision loss, and the Dent disease (DD) classical renal phenotype, that is, low molecular weight proteinuria (LMWP), hypercalciuria and nephrocalcinosis/nephrolithiasis. We propose that a subset of patients presenting as DD may represent unrecognized cases or mild forms of Donnai-Barrow/facio-oculo-acustico-renal (DB/FOAR) syndrome or be on the phenotypic continuum between the 2 conditions.
© 2018 John Wiley & Sons A/S. Published by John Wiley & Sons Ltd.
Publication types
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Case Reports
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Letter
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Research Support, N.I.H., Extramural
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Research Support, Non-U.S. Gov't
MeSH terms
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Adolescent
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Aged
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Agenesis of Corpus Callosum / diagnosis*
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Agenesis of Corpus Callosum / genetics
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Alleles
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Diagnosis, Differential
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Genetic Association Studies
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Genetic Predisposition to Disease
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Hearing Loss, Sensorineural / diagnosis*
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Hearing Loss, Sensorineural / genetics
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Hernias, Diaphragmatic, Congenital / diagnosis*
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Hernias, Diaphragmatic, Congenital / genetics
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Humans
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Hypercalciuria / diagnosis*
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Hypercalciuria / genetics
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Low Density Lipoprotein Receptor-Related Protein-2 / genetics
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Male
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Myopia / diagnosis*
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Myopia / genetics
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Nephrolithiasis / diagnosis*
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Nephrolithiasis / genetics
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Phenotype*
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Proteinuria / diagnosis*
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Proteinuria / genetics
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Renal Tubular Transport, Inborn Errors / diagnosis*
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Renal Tubular Transport, Inborn Errors / genetics
Substances
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LRP2 protein, human
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Low Density Lipoprotein Receptor-Related Protein-2