Voretigene neparvovec-rzyl (Luxturna) for inherited retinal dystrophy

Med Lett Drugs Ther. 2018 Mar 26;60(1543):53-55.
No abstract available

Keywords: adverse effects; dosage; drug interactions; efficacy; eye; safety.

MeSH terms

  • Dependovirus / genetics
  • Genetic Predisposition to Disease
  • Genetic Therapy / adverse effects
  • Genetic Therapy / economics
  • Genetic Therapy / methods*
  • Genetic Vectors
  • Heredity
  • Humans
  • Mutation
  • Retinal Dystrophies / diagnosis
  • Retinal Dystrophies / genetics
  • Retinal Dystrophies / metabolism
  • Retinal Dystrophies / therapy*
  • Treatment Outcome
  • cis-trans-Isomerases / biosynthesis
  • cis-trans-Isomerases / genetics*

Substances

  • retinoid isomerohydrolase
  • cis-trans-Isomerases