Recombinant Adeno-Associated Virus-Based Gene Therapy for Disorders Detected by Newborn Screening: Inherent Limitations of This Approach

Hum Gene Ther. 2018 Apr;29(4):401-402. doi: 10.1089/hum.2018.29064.trf.
No abstract available

Publication types

  • Editorial

MeSH terms

  • Dependovirus / genetics*
  • Genetic Diseases, Inborn / diagnosis*
  • Genetic Therapy / trends*
  • Genetic Vectors / genetics
  • Genetic Vectors / therapeutic use
  • Humans
  • Infant, Newborn
  • Neonatal Screening