Recombinant Adeno-Associated Virus-Based Gene Therapy for Disorders Detected by Newborn Screening: Inherent Limitations of This Approach
Hum Gene Ther
.
2018 Apr;29(4):401-402.
doi: 10.1089/hum.2018.29064.trf.
Author
Terence R Flotte
1
Affiliation
1
Editor-in Chief.
PMID:
29668376
DOI:
10.1089/hum.2018.29064.trf
No abstract available
Publication types
Editorial
MeSH terms
Dependovirus / genetics*
Genetic Diseases, Inborn / diagnosis*
Genetic Therapy / trends*
Genetic Vectors / genetics
Genetic Vectors / therapeutic use
Humans
Infant, Newborn
Neonatal Screening