Nanoparticles as Delivery Vehicles for the Treatment of Retinal Degenerative Diseases

Adv Exp Med Biol. 2018:1074:117-123. doi: 10.1007/978-3-319-75402-4_15.

Abstract

Over the last few years, huge progress has been made in the understanding of molecular mechanisms underlying the pathogenesis of retinal degenerative diseases. Such knowledge has led to the development of gene therapy approaches to treat these devastating disorders. Non-viral gene delivery has been recognized as a prospective treatment for retinal degenerative diseases. In this review, we will summarize the constituent characteristics and recent applications of three representative nanoparticles (NPs) in ocular therapy.

Keywords: Blindness; Lipid nanoparticles; Metal-based nanoparticles; Nanoparticles; Non-viral vectors; Ocular diseases; Polymer-based nanoparticles; Retinal degeneration.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't
  • Review

MeSH terms

  • Animals
  • Gene Transfer Techniques*
  • Genetic Therapy / methods*
  • Genetic Vectors / administration & dosage*
  • Humans
  • Liposomes / administration & dosage
  • Metal Nanoparticles / administration & dosage
  • Mice, Knockout
  • Nanoparticles / administration & dosage*
  • Polyethylene Glycols / administration & dosage
  • Polymers
  • Retinal Degeneration / therapy*
  • cis-trans-Isomerases / deficiency
  • cis-trans-Isomerases / genetics

Substances

  • Liposomes
  • Polymers
  • Polyethylene Glycols
  • retinoid isomerohydrolase
  • cis-trans-Isomerases