Emerging Gene Therapy Treatments for Inherited Retinal Diseases

Ophthalmic Surg Lasers Imaging Retina. 2018 Jul 1;49(7):472-478. doi: 10.3928/23258160-20180628-02.
No abstract available

MeSH terms

  • Dependovirus / genetics
  • Drug Approval
  • Genetic Therapy / methods*
  • Genetic Vectors
  • Humans
  • Retinal Dystrophies / genetics
  • Retinal Dystrophies / therapy*
  • United States
  • United States Food and Drug Administration
  • cis-trans-Isomerases / genetics

Substances

  • retinoid isomerohydrolase
  • cis-trans-Isomerases