Alpha-1 Antitrypsin Deficiency as a Candidate for Gene Editing

Hum Gene Ther. 2018 Aug;29(8):843-844. doi: 10.1089/hum.2018.29070.trf.
No abstract available

Publication types

  • Editorial

MeSH terms

  • Gene Editing*
  • Humans
  • alpha 1-Antitrypsin / genetics*
  • alpha 1-Antitrypsin Deficiency / genetics
  • alpha 1-Antitrypsin Deficiency / therapy*

Substances

  • SERPINA1 protein, human
  • alpha 1-Antitrypsin