Alpha-1 Antitrypsin Deficiency as a Candidate for Gene Editing
Hum Gene Ther
.
2018 Aug;29(8):843-844.
doi: 10.1089/hum.2018.29070.trf.
Author
Terence R Flotte
1
Affiliation
1
Editor-in-Chief.
PMID:
30096037
DOI:
10.1089/hum.2018.29070.trf
No abstract available
Publication types
Editorial
MeSH terms
Gene Editing*
Humans
alpha 1-Antitrypsin / genetics*
alpha 1-Antitrypsin Deficiency / genetics
alpha 1-Antitrypsin Deficiency / therapy*
Substances
SERPINA1 protein, human
alpha 1-Antitrypsin
Grants and funding
P01 HL131471/HL/NHLBI NIH HHS/United States