The role of patient and healthcare professionals in the era of new hemophilia treatments in developed and developing countries

Ther Adv Hematol. 2018 Jul 2;9(8):239-249. doi: 10.1177/2040620718784830. eCollection 2018 Aug.


Medical decisions in hemophilia care are primarily related to the type of factor replacement and treatment regimen. With the growing number of treatment options for patients with hemophilia, decision making is more complex and requires careful consideration of benefits, risks, and patient goals. Shared decision making and decision-aid tools facilitate patient and healthcare provider communication. In this review, the overall role of shared decision making in medicine is outlined, with special emphasis on models for practical implementation. Examples of shared decision making in hemophilia are outlined, and application to new therapeutics is discussed through a case-based approach.

Keywords: clotting factor; extended half-life; gene therapy; hemophilia; novel therapies; shared decision making.

Publication types

  • Review