HuC/D expression in small round cell tumors and neuroendocrine tumors: a useful tool for distinguishing neuroblastoma from childhood small round cell tumors

Hum Pathol. 2019 Mar:85:162-167. doi: 10.1016/j.humpath.2018.11.004. Epub 2018 Nov 20.

Abstract

The RNA-binding protein HuC/D displays a neuron-specific expression and is involved in neuronal differentiation and the maintenance of the nervous system. Here we investigated the diagnostic value of HuC/D in neuroblastomas. We evaluated 85 neuroblastic tumors: 81 neuroblastomas; 3 ganglioneuroblastomas, intermixed; 1 ganglioneuroma, maturing; and 101 other tumors consisting of 34 Ewing sarcomas, 14 nephroblastomas, 11 rhabdomyosarcomas, 15 pulmonary small cell carcinomas, 18 pancreatic neuroendocrine tumors, and 9 pheochromocytomas. Immunohistochemistry for HuC/D, PHOX2B, and tyrosine hydroxylase was performed. The immunoreactivity for HuC/D was semiquantified using the total score (TS; range, 0-8). HuC/D positivity was defined as a TS ≥6. The TS of the neuroblastic tumors (mean TS, 7.94) was significantly higher than those of the other small round cell tumors and neuroendocrine tumors (P < .001) except for the pheochromocytomas (mean TS, 6.89; P = .074). HuC/D was positive in all 85 neuroblastic tumors, 1 (2.9%) Ewing sarcoma, 1 (6.7%) pulmonary small cell carcinoma, and 8 (89%) pheochromocytomas. PHOX2B was positive in all of the neuroblastic tumors and pheochromocytomas. Tyrosine hydroxylase was positive in 80 (94%) neuroblastic tumors, 1 (9.1%) rhabdomyosarcoma, and all of the pheochromocytomas. Therefore, HuC/D serves as a highly sensitive diagnostic marker to distinguish neuroblastomas from other small round cell tumors. The combination of HuC/D and PHOX2B staining may be valuable for the diagnosis of neuroblastic tumors, especially in the assessment of small sections. HuC/D expression in tumors may be related to catecholamine production or a neural crest-derived cell origin.

Keywords: Differential diagnosis; HuC/D; Immunohistochemistry; Neuroblastoma; PHOX2B; Tyrosine hydroxylase.

MeSH terms

  • Adolescent
  • Adrenal Gland Neoplasms / diagnosis*
  • Adrenal Gland Neoplasms / metabolism
  • Adrenal Gland Neoplasms / pathology
  • Adult
  • Aged
  • Aged, 80 and over
  • Carcinoma, Small Cell / diagnosis*
  • Carcinoma, Small Cell / metabolism
  • Carcinoma, Small Cell / pathology
  • Child
  • Child, Preschool
  • Diagnosis, Differential
  • ELAV-Like Protein 3 / metabolism*
  • Female
  • Ganglioneuroblastoma / diagnosis*
  • Ganglioneuroblastoma / metabolism
  • Ganglioneuroblastoma / pathology
  • Homeodomain Proteins / metabolism
  • Humans
  • Infant
  • Infant, Newborn
  • Male
  • Middle Aged
  • Neuroblastoma / diagnosis*
  • Neuroblastoma / metabolism
  • Neuroblastoma / pathology
  • Neuroendocrine Tumors / diagnosis*
  • Neuroendocrine Tumors / metabolism
  • Neuroendocrine Tumors / pathology
  • Pancreatic Neoplasms / diagnosis*
  • Pancreatic Neoplasms / metabolism
  • Pancreatic Neoplasms / pathology
  • Pheochromocytoma / diagnosis*
  • Pheochromocytoma / metabolism
  • Pheochromocytoma / pathology
  • Sensitivity and Specificity
  • Transcription Factors / metabolism
  • Young Adult

Substances

  • ELAV-Like Protein 3
  • Homeodomain Proteins
  • NBPhox protein
  • Transcription Factors