Gene therapy targets sickle-cell disease

Nature. 2018 Dec;564(7735):S12-S13. doi: 10.1038/d41586-018-07646-w.
No abstract available

Keywords: Diseases; Gene therapy; Medical research; Stem cells.

MeSH terms

  • Anemia, Sickle Cell / genetics*
  • Anemia, Sickle Cell / therapy*
  • Child
  • Clinical Trials as Topic
  • Genetic Therapy* / economics
  • Humans
  • United States