Gene Therapy

N Engl J Med. 2019 Aug 1;381(5):455-464. doi: 10.1056/NEJMra1706910.
No abstract available

Publication types

  • Review

MeSH terms

  • Anemia, Sickle Cell / therapy
  • Animals
  • Dependovirus
  • Gene Transfer Techniques*
  • Genetic Therapy* / adverse effects
  • Genetic Therapy* / legislation & jurisprudence
  • Genetic Therapy* / methods
  • Genetic Vectors
  • Government Regulation
  • Humans
  • Lentivirus
  • Muscular Atrophy, Spinal / therapy
  • Thalassemia / therapy
  • Vision Disorders / genetics
  • Vision Disorders / therapy