Why rare genetic diseases are a logical focus for RNA therapies
Nature
.
2019 Oct;574(7778):S16-S18.
doi: 10.1038/d41586-019-03075-5.
Author
Liam Drew
PMID:
31619800
DOI:
10.1038/d41586-019-03075-5
No abstract available
Keywords:
Drug discovery; Therapeutics.
MeSH terms
Genetic Diseases, Inborn / therapy*
Humans
Molecular Targeted Therapy / standards
Molecular Targeted Therapy / trends*
RNA / therapeutic use*
Rare Diseases / therapy*
Substances
RNA