Insertion of an Alu Element in Thyroglobulin Gene as a Novel Cause of Congenital Hypothyroidism

Thyroid. 2020 May;30(5):780-782. doi: 10.1089/thy.2019.0636. Epub 2020 Feb 3.

Abstract

The thyroglobulin (TG) gene encodes a protein required for thyroid hormone synthesis and iodine storage. Deleterious TG mutations produce congenital hypothyroidism (CH) often presenting with undetectable serum TG. Alu elements, common throughout the human genome, have a poly(dA) region in the 3' end of the strand. Herein two of four siblings of a consanguineous Sudanese family with CH, goiter, high initial serum thyrotropin, and undetectable TG were found to have a novel frameshift insertion of an Alu element within an exon of the TG gene: c.7909ins p.Y3637Ffs. This report demonstrates a novel Alu element insertion within TG causing CH.

Keywords: Alu element; TG; congenital hypothyroidism; goiter; novel mutation; thyroglobulin.

Publication types

  • Case Reports
  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Alu Elements*
  • Child
  • Child, Preschool
  • Congenital Hypothyroidism / blood
  • Congenital Hypothyroidism / drug therapy
  • Congenital Hypothyroidism / genetics*
  • Female
  • Humans
  • Mutagenesis, Insertional*
  • Thyroglobulin / blood
  • Thyroglobulin / genetics*
  • Thyroxine / therapeutic use

Substances

  • Thyroglobulin
  • Thyroxine