Triple Therapy for Cystic Fibrosis with a Phe508del CFTR Mutation

N Engl J Med. 2020 Feb 13;382(7):684. doi: 10.1056/NEJMc1916747.
No abstract available

Publication types

  • Letter
  • Comment

MeSH terms

  • Alleles
  • Aminophenols
  • Benzodioxoles
  • Cystic Fibrosis / genetics*
  • Cystic Fibrosis Transmembrane Conductance Regulator / genetics
  • Humans
  • Indoles
  • Mutation
  • Quinolones

Substances

  • Aminophenols
  • Benzodioxoles
  • Indoles
  • Quinolones
  • tezacaftor
  • Cystic Fibrosis Transmembrane Conductance Regulator
  • ivacaftor