Optical induction of autophagy via Transcription factor EB (TFEB) reduces pathological tau in neurons

PLoS One. 2020 Mar 24;15(3):e0230026. doi: 10.1371/journal.pone.0230026. eCollection 2020.

Abstract

Pathological accumulation of microtubule associated protein tau in neurons is a major neuropathological hallmark of Alzheimer's disease (AD) and related tauopathies. Several attempts have been made to promote clearance of pathological tau (p-Tau) from neurons. Transcription factor EB (TFEB) has shown to clear p-Tau from neurons via autophagy. However, sustained TFEB activation and autophagy can create burden on cellular bioenergetics and can be deleterious. Here, we modified previously described two-plasmid systems of Light Activated Protein (LAP) from bacterial transcription factor-EL222 and Light Responsive Element (LRE) to encode TFEB. Upon blue-light (465 nm) illumination, the conformation changes in LAP induced LRE-driven expression of TFEB, its nuclear entry, TFEB-mediated expression of autophagy-lysosomal genes and clearance of p-Tau from neuronal cells and AD patient-derived human iPSC-neurons. Turning the blue-light off reversed the expression of TFEB-target genes and attenuated p-Tau clearance. Together, these results suggest that optically regulated TFEB expression unlocks the potential of opto-therapeutics to treat AD and other dementias.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Autophagy*
  • HEK293 Cells
  • Humans
  • Light*
  • Neurons / metabolism
  • Neurons / pathology*
  • Neurons / radiation effects*
  • Nuclear Localization Signals / metabolism
  • Tauopathies / metabolism
  • Tauopathies / pathology
  • tau Proteins / chemistry
  • tau Proteins / metabolism*

Substances

  • Nuclear Localization Signals
  • tau Proteins