Boosting delivery of rare disease therapies: the IRDiRC Orphan Drug Development Guidebook

Nat Rev Drug Discov. 2020 Aug;19(8):495-496. doi: 10.1038/d41573-020-00060-w.

Authors

Anneliene Hechtelt Jonker, Virginie Hivert, Michela Gabaldo, Liliana Batista, Daniel O'Connor, Annemieke Aartsma-Rus, Simon Day, Ken Sakushima, Diego Ardigo

PMID: 32313251
DOI: 10.1038/d41573-020-00060-w

No abstract available

Publication types

News

MeSH terms

Humans
Orphan Drug Production*
Rare Diseases / drug therapy*