Givosiran - Running RNA Interference to Fight Porphyria Attacks

N Engl J Med. 2020 Jun 11;382(24):2366-2367. doi: 10.1056/NEJMe2010986.
No abstract available

Publication types

  • Editorial
  • Comment

MeSH terms

  • Acetylgalactosamine / analogs & derivatives
  • Humans
  • Porphyria, Acute Intermittent*
  • Porphyrias*
  • Pyrrolidines
  • RNA Interference
  • RNAi Therapeutics
  • Running*

Substances

  • Pyrrolidines
  • Acetylgalactosamine
  • givosiran