Abstract
FGFR2 rearrangements resulting in dysregulated signaling are drivers of cholangiocarcinoma (CCA) tumorigenesis, and occur almost exclusively in intrahepatic CCA. Pemigatinib, a selective, potent, oral inhibitor of FGFR1-3, has demonstrated efficacy and safety in a Phase II study of patients with previously treated locally advanced/metastatic CCA harboring FGFR2 fusions/rearrangements. We describe the study design of FIGHT-302, an open-label, randomized, active-controlled, multicenter, global, Phase III study comparing the efficacy and safety of first-line pemigatinib versus gemcitabine plus cisplatin in patients with advanced CCA with FGFR2 rearrangements (NCT03656536). The primary end point is progression-free survival; secondary end points are objective response rate, overall survival, duration of response, disease control rate, safety and quality of life. Clinical Trial Registration: NCT03656536 (ClinicalTrials.gov).
Keywords:
FGFR; INCB054828; cholangiocarcinoma; pemigatinib.
Publication types
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Clinical Trial, Phase III
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Multicenter Study
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Randomized Controlled Trial
MeSH terms
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Antineoplastic Combined Chemotherapy Protocols / adverse effects
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Antineoplastic Combined Chemotherapy Protocols / therapeutic use*
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Bile Duct Neoplasms / diagnosis
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Bile Duct Neoplasms / drug therapy*
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Bile Duct Neoplasms / genetics*
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Bile Duct Neoplasms / mortality
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Biomarkers, Tumor
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Cholangiocarcinoma / diagnosis
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Cholangiocarcinoma / drug therapy*
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Cholangiocarcinoma / genetics*
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Cholangiocarcinoma / mortality
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Cisplatin / administration & dosage
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Clinical Protocols
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Deoxycytidine / administration & dosage
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Deoxycytidine / analogs & derivatives
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Female
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Gemcitabine
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Gene Rearrangement*
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Humans
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Male
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Molecular Targeted Therapy
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Morpholines / administration & dosage
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Morpholines / adverse effects
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Morpholines / therapeutic use*
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Mutation
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Pyrimidines / administration & dosage
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Pyrimidines / adverse effects
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Pyrimidines / therapeutic use*
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Pyrroles / administration & dosage
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Pyrroles / adverse effects
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Pyrroles / therapeutic use*
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Receptor, Fibroblast Growth Factor, Type 2 / genetics*
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Research Design
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Treatment Outcome
Substances
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Biomarkers, Tumor
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Morpholines
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Pyrimidines
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Pyrroles
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Deoxycytidine
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FGFR2 protein, human
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Receptor, Fibroblast Growth Factor, Type 2
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Cisplatin
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pemigatinib
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Gemcitabine
Associated data
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ClinicalTrials.gov/NCT03656536