Golodirsen (Vyondys 53) for Duchenne muscular dystrophy

Med Lett Drugs Ther. 2020 Jul 27;62(1603):119-120.
No abstract available

Keywords: Duchenne muscular dystrophy; Emflaza; Exondys 51; Vyondys 53; adverse effects; deflazacort; dosage; efficacy; eteplirsen; golodirsen; prednisone; safety.

MeSH terms

  • Humans
  • Muscular Dystrophy, Duchenne / drug therapy*
  • Oligonucleotides, Antisense / administration & dosage
  • Oligonucleotides, Antisense / adverse effects
  • Oligonucleotides, Antisense / therapeutic use*

Substances

  • Oligonucleotides, Antisense