Gene Therapy for Respiratory Diseases: Progress and a Changing Context

Hum Gene Ther. 2020 Sep;31(17-18):911-916. doi: 10.1089/hum.2020.142.
No abstract available

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Cystic Fibrosis / genetics
  • Cystic Fibrosis / therapy*
  • Cystic Fibrosis Transmembrane Conductance Regulator / genetics*
  • Dependovirus / genetics*
  • Gene Editing*
  • Genetic Therapy / methods*
  • Genetic Vectors / administration & dosage*
  • Genetic Vectors / genetics
  • Humans

Substances

  • CFTR protein, human
  • Cystic Fibrosis Transmembrane Conductance Regulator