A defined structural unit enables de novo design of small-molecule-binding proteins

Science. 2020 Sep 4;369(6508):1227-1233. doi: 10.1126/science.abb8330.

Abstract

The de novo design of proteins that bind highly functionalized small molecules represents a great challenge. To enable computational design of binders, we developed a unit of protein structure-a van der Mer (vdM)-that maps the backbone of each amino acid to statistically preferred positions of interacting chemical groups. Using vdMs, we designed six de novo proteins to bind the drug apixaban; two bound with low and submicromolar affinity. X-ray crystallography and mutagenesis confirmed a structure with a precisely designed cavity that forms favorable interactions in the drug-protein complex. vdMs may enable design of functional proteins for applications in sensing, medicine, and catalysis.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Drug Evaluation, Preclinical*
  • Fibrinolytic Agents / chemistry
  • Protein Binding
  • Protein Engineering*
  • Protein Structure, Secondary
  • Proteins / chemistry*
  • Proteins / genetics
  • Pyrazoles / chemistry
  • Pyridones / chemistry
  • Small Molecule Libraries / chemistry*

Substances

  • Fibrinolytic Agents
  • Proteins
  • Pyrazoles
  • Pyridones
  • Small Molecule Libraries
  • apixaban