Activity profiling and crystal structures of inhibitor-bound SARS-CoV-2 papain-like protease: A framework for anti-COVID-19 drug design

Sci Adv. 2020 Oct 16;6(42):eabd4596. doi: 10.1126/sciadv.abd4596. Print 2020 Oct.

Abstract

Viral papain-like cysteine protease (PLpro, NSP3) is essential for SARS-CoV-2 replication and represents a promising target for the development of antiviral drugs. Here, we used a combinatorial substrate library and performed comprehensive activity profiling of SARS-CoV-2 PLpro. On the scaffold of the best hits from positional scanning, we designed optimal fluorogenic substrates and irreversible inhibitors with a high degree of selectivity for SARS PLpro. We determined crystal structures of two of these inhibitors in complex with SARS-CoV-2 PLpro that reveals their inhibitory mechanisms and provides a molecular basis for the observed substrate specificity profiles. Last, we demonstrate that SARS-CoV-2 PLpro harbors deISGylating activity similar to SARSCoV-1 PLpro but its ability to hydrolyze K48-linked Ub chains is diminished, which our sequence and structure analysis provides a basis for. Together, this work has revealed the molecular rules governing PLpro substrate specificity and provides a framework for development of inhibitors with potential therapeutic value or drug repurposing.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, Non-P.H.S.

MeSH terms

  • Amino Acid Sequence
  • Betacoronavirus / enzymology*
  • Betacoronavirus / isolation & purification
  • Binding Sites
  • COVID-19
  • Catalytic Domain
  • Coronavirus 3C Proteases
  • Coronavirus Infections / pathology
  • Coronavirus Infections / virology
  • Crystallography, X-Ray
  • Cysteine Endopeptidases / genetics
  • Cysteine Endopeptidases / metabolism
  • Drug Design*
  • Humans
  • Kinetics
  • Molecular Dynamics Simulation
  • Oligopeptides / chemistry
  • Oligopeptides / metabolism
  • Pandemics
  • Pneumonia, Viral / pathology
  • Pneumonia, Viral / virology
  • Protease Inhibitors / chemistry*
  • Protease Inhibitors / metabolism
  • Recombinant Proteins / biosynthesis
  • Recombinant Proteins / chemistry
  • Recombinant Proteins / isolation & purification
  • SARS-CoV-2
  • Substrate Specificity
  • Ubiquitins / metabolism
  • Viral Nonstructural Proteins / antagonists & inhibitors*
  • Viral Nonstructural Proteins / genetics
  • Viral Nonstructural Proteins / metabolism

Substances

  • Oligopeptides
  • Protease Inhibitors
  • Recombinant Proteins
  • Ubiquitins
  • Viral Nonstructural Proteins
  • Cysteine Endopeptidases
  • Coronavirus 3C Proteases