The once and future gene therapy

Nat Commun. 2020 Nov 16;11(1):5820. doi: 10.1038/s41467-020-19505-2.


Gene therapy is at an inflection point. Recent successes in genetic medicine have paved the path for a broader second wave of therapies and laid the foundation for next-generation technologies. This comment summarizes recent advances and expectations for the near future.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Clinical Trials as Topic
  • Disease / genetics
  • Gene Editing
  • Genetic Therapy*
  • Humans