Integrative functional genomic analysis of intron retention in human and mouse brain with Alzheimer's disease

Alzheimers Dement. 2021 Jun;17(6):984-1004. doi: 10.1002/alz.12254. Epub 2021 Jan 21.

Abstract

Intron retention (IR) has been implicated in the pathogenesis of complex diseases such as cancers; its association with Alzheimer's disease (AD) remains unexplored. We performed genome-wide analysis of IR through integrating genetic, transcriptomic, and proteomic data of AD subjects and mouse models from the Accelerating Medicines Partnership-Alzheimer's Disease project. We identified 4535 and 4086 IR events in 2173 human and 1736 mouse genes, respectively. Quantitation of IR enabled the identification of differentially expressed genes that conventional exon-level approaches did not reveal. There were significant correlations of intron expression within innate immune genes, like HMBOX1, with AD in humans. Peptides with a high probability of translation from intron-retained mRNAs were identified using mass spectrometry. Further, we established AD-specific intron expression Quantitative Trait Loci, and identified splicing-related genes that may regulate IR. Our analysis provides a novel resource for the search for new AD biomarkers and pathological mechanisms.

Keywords: Alzheimer's disease; alternative splicing; gene expression; integrative analysis; intron retention.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Alzheimer Disease* / genetics
  • Alzheimer Disease* / pathology
  • Animals
  • Autopsy*
  • Brain / pathology*
  • Disease Models, Animal*
  • Genomics*
  • Homeodomain Proteins / genetics
  • Humans
  • Introns / genetics*
  • Mice
  • Proteomics
  • Quantitative Trait Loci
  • Transcriptome

Substances

  • Hmbox1 protein, mouse
  • Homeodomain Proteins