A plethora of gene therapies for hemoglobinopathies

Nat Med. 2021 Feb;27(2):202-204. doi: 10.1038/s41591-021-01235-7.
No abstract available

Publication types

  • Research Support, N.I.H., Intramural
  • Comment

MeSH terms

  • Anemia, Sickle Cell* / genetics
  • Anemia, Sickle Cell* / therapy
  • CRISPR-Cas Systems
  • Gene Editing
  • Hemoglobinopathies* / genetics
  • Hemoglobinopathies* / therapy
  • Humans
  • beta-Thalassemia*