New disease modifying therapies for two genetic childhood-onset neurometabolic disorders (metachromatic leucodystrophy and adrenoleucodystrophy)
Neurol Sci
.
2021 Jul;42(7):2603-2606.
doi: 10.1007/s10072-021-05412-x.
Epub 2021 Jul 1.
Authors
Antonio Federico
1
,
Marianne de Visser
2
Affiliations
1
Department of Medicine, Surgery and Neurosciences, Medical School, University of Siena, Viale Bracci 2, 53100, Siena, Italy. antonio.federico@unisi.it.
2
Department of Neurology, Amsterdam University Medical Centres, Amsterdam, The Netherlands.
PMID:
34212263
DOI:
10.1007/s10072-021-05412-x
No abstract available
Publication types
Editorial
MeSH terms
Adrenoleukodystrophy* / genetics
Adrenoleukodystrophy* / therapy
Child
Humans
Leukodystrophy, Metachromatic*