Maximising returns: combining newborn screening with gene therapy for spinal muscular atrophy

J Neurol Neurosurg Psychiatry. 2021 Dec;92(12):1252. doi: 10.1136/jnnp-2021-327459. Epub 2021 Jul 28.
No abstract available

Keywords: health economics; spinal muscular atrophy.

Publication types

  • Editorial
  • Comment

MeSH terms

  • Genetic Testing
  • Genetic Therapy
  • Humans
  • Infant, Newborn
  • Muscular Atrophy, Spinal* / diagnosis
  • Muscular Atrophy, Spinal* / genetics
  • Muscular Atrophy, Spinal* / therapy
  • Neonatal Screening*