Emerging Therapeutic Strategies for Fragile X Syndrome: Q&A

ACS Chem Neurosci. 2022 Dec 21;13(24):3544-3546. doi: 10.1021/acschemneuro.2c00674. Epub 2022 Dec 7.

Abstract

Understanding how best to treat aspects of Fragile X syndrome has the potential to improve the quality of life of affected individuals. Such an effective therapy has, as yet, remained elusive. In this article, we ask those researching or affected by Fragile X syndrome their views on the current state of research and from where they feel the most likely therapy may emerge.

Keywords: Fragile X syndrome; arbaclofen; fragile X messenger ribonucleoprotein 1; neurodevelopmental conditions; phosphodiesterase; somatosensation.

MeSH terms

  • Fragile X Mental Retardation Protein / genetics
  • Fragile X Syndrome* / drug therapy
  • Humans
  • Quality of Life

Substances

  • Fragile X Mental Retardation Protein