Challenges in the clinical advancement of cell therapies for Parkinson's disease

Nat Biomed Eng. 2023 Apr;7(4):370-386. doi: 10.1038/s41551-022-00987-y. Epub 2023 Jan 12.

Abstract

Cell therapies as potential treatments for Parkinson's disease first gained traction in the 1980s, owing to the clinical success of trials that used transplants of foetal midbrain dopaminergic tissue. However, the poor standardization of the tissue for grafting, and constraints on its availability and ethical use, have hindered this treatment strategy. Recent advances in stem-cell technologies and in the understanding of the development of dopaminergic neurons have enabled preclinical advancements of promising stem-cell therapies. To move these therapies to the clinic, appropriate levels of safety screening, as well as optimization of the cell products and the scalability of their manufacturing, will be required. In this Review, we discuss how challenges pertaining to cell sources, functional and safety testing, manufacturing and storage, and clinical-trial design are being addressed to advance the translational and clinical development of cell therapies for Parkinson's disease.

Publication types

  • Review
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Cell- and Tissue-Based Therapy
  • Dopaminergic Neurons / physiology
  • Dopaminergic Neurons / transplantation
  • Humans
  • Parkinson Disease* / therapy
  • Stem Cell Transplantation