1 UCL Great Ormond Street Institute of Child Health, London, UK.
2 Biomedical Innovation Unit, Centro de Investigaciones Energéticas, Medioambientales y Tecnológicas (CIEMAT), Centro Investigación Biomédica en Red de Enfermedades Raras (CIBERER) and IIS Fundación Jiménez Díaz, Madrid, Spain.
3 Division of Immunology and Allergy, University Hospital of Lausanne and Lausanne University, Lausanne, Switzerland.
4 Imagine Institute, Paris, France.
5 San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute and Vita-Salute San Raffaele University, Milan, Italy.
6 Willem-Alexander Children's Hospital, Department of Pediatrics, Stem Cell Transplantation Program, Leiden University Medical Center, Leiden, The Netherlands.
7 UCL Great Ormond Street Institute of Child Health, London, UK. c.booth@ucl.ac.uk.