Access to gene therapy for rare diseases when commercialization is not fit for purpose

Nat Med. 2023 Mar;29(3):518-519. doi: 10.1038/s41591-023-02208-8.
No abstract available

Publication types

  • Letter

MeSH terms

  • Genetic Therapy*
  • Humans
  • Rare Diseases* / genetics
  • Rare Diseases* / therapy