Every little bit helps: A single-residue switch in a vascular AAV enables blood-brain barrier penetration
Mol Ther Methods Clin Dev
.
2023 May 16:29:364-365.
doi: 10.1016/j.omtm.2023.04.007.
eCollection 2023 Jun 8.
Authors
Dirk Grimm
1
,
Mathieu Nonnenmacher
2
Affiliations
1
Department of Infectious Diseases/Virology, Section Viral Vector Technologies, Medical Faculty, BioQuant, Heidelberg University, Im Neuenheimer Feld 267, 69120 Heidelberg, Germany.
2
Voyager Therapeutics, 64 Sidney Street, Cambridge, MA 02139, USA.
PMID:
37214312
PMCID:
PMC10199398
DOI:
10.1016/j.omtm.2023.04.007
No abstract available
Publication types
News