Dersimelagon in Erythropoietic Protoporphyrias. Reply
N Engl J Med
.
2023 Jun 29;388(26):2492-2493.
doi: 10.1056/NEJMc2305601.
Authors
Manisha Balwani
1
,
Robert J Desnick
1
,
Kirstine Belongie
2
Affiliations
1
Icahn School of Medicine at Mount Sinai, New York, NY.
2
Mitsubishi Tanabe Pharma America, Jersey City, NJ kirstine_belongie@mt-pharma-us.com.
PMID:
37379151
DOI:
10.1056/NEJMc2305601
No abstract available
Publication types
Letter
Comment
MeSH terms
Humans
Protoporphyria, Erythropoietic* / diagnosis
Protoporphyria, Erythropoietic* / genetics