Lessons and future directions for GBA1-targeting therapies

Lancet Neurol. 2023 Aug;22(8):644-645. doi: 10.1016/S1474-4422(23)00217-X.
No abstract available

Publication types

  • Comment

MeSH terms

  • Glucosylceramidase* / genetics
  • Glucosylceramidase* / therapeutic use
  • Humans
  • Mutation
  • Parkinson Disease*
  • alpha-Synuclein

Substances

  • Glucosylceramidase
  • alpha-Synuclein