Stem Cell Gene Editing Improved Sickle Cell Disease Outcomes

JAMA. 2023 Oct 3;330(13):1218. doi: 10.1001/jama.2023.17177.
No abstract available

MeSH terms

  • Anemia, Sickle Cell* / genetics
  • Anemia, Sickle Cell* / therapy
  • CRISPR-Cas Systems / genetics
  • Gene Editing* / methods
  • Hematopoietic Stem Cell Transplantation*
  • Humans
  • Stem Cells*