Discontinued CRISPR gene therapy for sickle-cell disease improves symptoms

Nat Med. 2023 Nov;29(11):2669-2670. doi: 10.1038/d41591-023-00088-6.
No abstract available

Publication types

  • News

MeSH terms

  • Anemia, Sickle Cell* / genetics
  • Anemia, Sickle Cell* / therapy
  • CRISPR-Cas Systems / genetics
  • Clustered Regularly Interspaced Short Palindromic Repeats*
  • Gene Editing
  • Genetic Therapy
  • Humans