UK regulator approves "groundbreaking" gene treatment for sickle cell and β thalassaemia

BMJ. 2023 Nov 16:383:2706. doi: 10.1136/bmj.p2706.
No abstract available

MeSH terms

  • Anemia, Sickle Cell* / genetics
  • Anemia, Sickle Cell* / therapy
  • Humans
  • United Kingdom
  • beta-Thalassemia* / genetics
  • beta-Thalassemia* / therapy