Sickle Cell Disease Approvals Include First CRISPR Gene Editing Therapy

JAMA. 2024 Jan 23;331(4):280. doi: 10.1001/jama.2023.26113.
No abstract available

MeSH terms

  • Anemia, Sickle Cell* / genetics
  • Anemia, Sickle Cell* / therapy
  • CRISPR-Cas Systems*
  • Clustered Regularly Interspaced Short Palindromic Repeats
  • Gene Editing* / methods
  • Genetic Therapy* / methods
  • Humans