Vision on gyrate atrophy: why treat the liver?

EMBO Mol Med. 2024 Jan;16(1):8-9. doi: 10.1038/s44321-023-00002-0. Epub 2023 Dec 14.

Abstract

Gyrate Atrophy of the Choroid and Retina (GACR) currently lacks any effective treatment and a highly restricted, yet cumbersome, low-arginine diet is the only available therapeutic option. In our work, we found that replacement of ornithine-aminotransferase (OAT) activity in the liver lowers ornithine concentrations in the blood and the eye, thus improving retinal structure and function (Boffa et al, 2023).

Publication types

  • Letter

MeSH terms

  • Atrophy
  • Gyrate Atrophy*
  • Humans
  • Liver
  • Retina