Spending on Targeted Therapies for Duchenne Muscular Dystrophy

JAMA. 2024 Apr 2;331(13):1151-1153. doi: 10.1001/jama.2024.2776.
No abstract available

Plain language summary

This study estimates public and private spending on genetically targeted treatments for Duchenne muscular dystrophy during years in which the drugs were marketed without completed confirmatory studies.

Publication types

  • Research Support, Non-U.S. Gov't
  • Letter

MeSH terms

  • Humans
  • Molecular Targeted Therapy* / economics
  • Muscular Dystrophy, Duchenne* / drug therapy
  • Muscular Dystrophy, Duchenne* / economics