FDA approves an HDAC inhibitor for Duchenne muscular dystrophy

Nat Rev Drug Discov. 2024 May;23(5):329. doi: 10.1038/d41573-024-00066-8.
No abstract available

Publication types

  • News

MeSH terms

  • Drug Approval*
  • Histone Deacetylase Inhibitors* / pharmacology
  • Histone Deacetylase Inhibitors* / therapeutic use
  • Humans
  • Muscular Dystrophy, Duchenne* / drug therapy
  • United States
  • United States Food and Drug Administration*

Substances

  • Histone Deacetylase Inhibitors