Extending Gene Medicines to All in Need

N Engl J Med. 2024 May 9;390(18):1721-1722. doi: 10.1056/NEJMe2403104. Epub 2024 Apr 24.

Authors

Joseph M McCune¹, Hans-Peter Kiem¹

Affiliation

¹ From the Global Health Division, Bill and Melinda Gates Foundation (J.M.M.), and the Fred Hutchinson Cancer Center and University of Washington School of Medicine (H.-P.K.) - all in Seattle.

PMID: 38657269
DOI: 10.1056/NEJMe2403104

No abstract available

Publication types

Editorial

MeSH terms

Anemia, Sickle Cell / genetics
Anemia, Sickle Cell / therapy
Gene Editing* / methods
Genetic Therapy* / methods
Health Services Accessibility*
Hematopoietic Stem Cell Transplantation* / methods
Hematopoietic Stem Cells / physiology
Hemoglobinopathies* / genetics
Hemoglobinopathies* / therapy
Humans
United States
beta-Thalassemia / genetics
beta-Thalassemia / therapy