Oral Iptacopan in Paroxysmal Nocturnal Hemoglobinuria

N Engl J Med. 2024 Jun 6;390(21):2032-2033. doi: 10.1056/NEJMc2404445.
No abstract available

Publication types

  • Letter
  • Comment

MeSH terms

  • Administration, Oral
  • Adult
  • Complement Factor B* / antagonists & inhibitors
  • Female
  • Hematologic Agents* / administration & dosage
  • Hematologic Agents* / adverse effects
  • Hematologic Agents* / therapeutic use
  • Hemoglobinuria, Paroxysmal* / complications
  • Hemoglobinuria, Paroxysmal* / drug therapy
  • Humans
  • Male
  • Peptides, Cyclic

Substances

  • Complement Factor B
  • Hematologic Agents
  • pegcetacoplan
  • Peptides, Cyclic