Thalassaemia: NICE recommends "life changing" gene editing therapy

BMJ. 2024 Aug 8:386:q1771. doi: 10.1136/bmj.q1771.
No abstract available

Publication types

  • News

MeSH terms

  • Gene Editing* / ethics
  • Gene Editing* / methods
  • Genetic Therapy* / methods
  • Humans
  • Practice Guidelines as Topic
  • Thalassemia* / genetics
  • Thalassemia* / therapy
  • United Kingdom