Sickle cell drug is withdrawn over safety concerns just months after rollout

BMJ. 2024 Oct 1:387:q2147. doi: 10.1136/bmj.q2147.
No abstract available

Publication types

  • News

MeSH terms

  • Anemia, Sickle Cell / drug therapy
  • Antisickling Agents* / adverse effects
  • Antisickling Agents* / therapeutic use
  • Benzaldehydes
  • Humans
  • Pyrazines
  • Pyrazoles
  • Safety-Based Drug Withdrawals*

Substances

  • Antisickling Agents
  • Pyrazines
  • voxelotor
  • Benzaldehydes
  • Pyrazoles