Siponimod inhibits microglial inflammasome activation

Neurosci Res. 2025 Apr:213:138-145. doi: 10.1016/j.neures.2025.02.002. Epub 2025 Feb 5.

Abstract

Siponimod is the first oral drug approved for active secondary progressive multiple sclerosis. It acts as a functional antagonist of sphingosine-1-phosphate (S1P) receptor 1 (S1P1) through S1P1 internalization, and also serves an agonist of S1P5; however, the detailed mechanisms of its therapeutic effects on glial cells have yet to be elucidated. In this study, we investigated the anti-inflammatory mechanism of siponimod in microglia. Pretreatment with either siponimod or the S1P1 antagonist W146 significantly suppressed the production of interleukin-1β in activated microglia stimulated with lipopolysaccharide plus nigericin, an inflammasome activator. Furthermore, siponimod treatment reduced the protein levels of cleaved caspase-1 and inhibited the formation of aggregates of apoptosis-associated speck-like protein containing a C-terminal caspase recruitment domain (ASC specks) in microglia. Our data indicate that siponimod achieves its anti-inflammatory effects by inhibiting inflammasome activation in microglia via S1P1 antagonism. This process is inferred to play a crucial role in mitigating the secondary progression of multiple sclerosis, where microglial activation in the gray matter is considered a key pathological factor.

Keywords: Cytokine; Inflammasome; Microglia; Multiple sclerosis; Siponimod; Sphingosine-1-phosphate receptor 1.

MeSH terms

  • Animals
  • Azetidines* / pharmacology
  • Benzyl Compounds* / pharmacology
  • Caspase 1 / metabolism
  • Cells, Cultured
  • Inflammasomes* / drug effects
  • Inflammasomes* / metabolism
  • Interleukin-1beta / metabolism
  • Mice
  • Mice, Inbred C57BL
  • Microglia* / drug effects
  • Microglia* / metabolism
  • Sphingosine 1 Phosphate Receptor Modulators* / pharmacology

Substances

  • Inflammasomes
  • siponimod
  • Azetidines
  • Benzyl Compounds
  • Sphingosine 1 Phosphate Receptor Modulators
  • Caspase 1
  • Interleukin-1beta